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Proximal Hereditary Motor Neuropathy Type I

MedGen UID:
21913
Concept ID:
C0043116
Disease or Syndrome
Synonym: HMN (Hereditary Motor Neuropathy) Proximal Type I

Term Hierarchy

CClinical test,  RResearch test,  OOMIM,  GGeneReviews,  VClinVar  
  • CROGVProximal Hereditary Motor Neuropathy Type I
Follow this link to review classifications for Proximal Hereditary Motor Neuropathy Type I in Orphanet.

Professional guidelines

PubMed

Beloribi-Djefaflia S, Attarian S
Rev Neurol (Paris) 2023 Jan-Feb;179(1-2):35-48. Epub 2022 Dec 30 doi: 10.1016/j.neurol.2022.11.006. PMID: 36588067
Yiu EM, Bray P, Baets J, Baker SK, Barisic N, de Valle K, Estilow T, Farrar MA, Finkel RS, Haberlová J, Kennedy RA, Moroni I, Nicholson GA, Ramchandren S, Reilly MM, Rose K, Shy ME, Siskind CE, Yum SW, Menezes MP, Ryan MM, Burns J
J Neurol Neurosurg Psychiatry 2022 May;93(5):530-538. Epub 2022 Feb 9 doi: 10.1136/jnnp-2021-328483. PMID: 35140138
Stino AM, Naddaf E, Dyck PJ, Dyck PJB
Muscle Nerve 2021 Feb;63(2):157-169. Epub 2020 Sep 11 doi: 10.1002/mus.27046. PMID: 32914902

Recent clinical studies

Etiology

Beloribi-Djefaflia S, Attarian S
Rev Neurol (Paris) 2023 Jan-Feb;179(1-2):35-48. Epub 2022 Dec 30 doi: 10.1016/j.neurol.2022.11.006. PMID: 36588067
Murala S, Nagarajan E, Bollu PC
Neurol Sci 2021 Mar;42(3):883-894. Epub 2021 Jan 13 doi: 10.1007/s10072-020-04981-7. PMID: 33439395
Barreto LC, Oliveira FS, Nunes PS, de França Costa IM, Garcez CA, Goes GM, Neves EL, de Souza Siqueira Quintans J, de Souza Araújo AA
Neuroepidemiology 2016;46(3):157-65. Epub 2016 Feb 6 doi: 10.1159/000443706. PMID: 26849231
Sman AD, Hackett D, Fiatarone Singh M, Fornusek C, Menezes MP, Burns J
J Peripher Nerv Syst 2015 Dec;20(4):347-62. doi: 10.1111/jns.12116. PMID: 26010435
Szigeti K, Lupski JR
Eur J Hum Genet 2009 Jun;17(6):703-10. Epub 2009 Mar 11 doi: 10.1038/ejhg.2009.31. PMID: 19277060Free PMC Article

Diagnosis

Kramarz C, Rossor AM
J Neurol 2022 Sep;269(9):5187-5191. Epub 2022 May 21 doi: 10.1007/s00415-022-11164-1. PMID: 35596796Free PMC Article
Attarian S, Fatehi F, Rajabally YA, Pareyson D
J Neurol 2020 Aug;267(8):2198-2206. Epub 2019 Apr 15 doi: 10.1007/s00415-019-09319-8. PMID: 30989370
Rudnik-Schöneborn S, Auer-Grumbach M, Senderek J
Neuropediatrics 2017 Aug;48(4):282-293. Epub 2017 Jun 8 doi: 10.1055/s-0037-1603518. PMID: 28597455
Rinaldi R, Patel A
PM R 2013 May;5(5 Suppl):S63-73. Epub 2013 Mar 28 doi: 10.1016/j.pmrj.2013.03.028. PMID: 23542772
Kleopa KA, Scherer SS
Neurol Clin 2002 Aug;20(3):679-709. doi: 10.1016/s0733-8619(01)00016-0. PMID: 12432826

Therapy

Stino AM, Naddaf E, Dyck PJ, Dyck PJB
Muscle Nerve 2021 Feb;63(2):157-169. Epub 2020 Sep 11 doi: 10.1002/mus.27046. PMID: 32914902
Lallemant-Dudek P, Durr A
Rev Neurol (Paris) 2021 May;177(5):550-556. Epub 2020 Aug 15 doi: 10.1016/j.neurol.2020.07.001. PMID: 32807405
Morena J, Gupta A, Hoyle JC
Int J Mol Sci 2019 Jul 12;20(14) doi: 10.3390/ijms20143419. PMID: 31336816Free PMC Article
Corrado B, Ciardi G, Bargigli C
Medicine (Baltimore) 2016 Apr;95(17):e3278. doi: 10.1097/MD.0000000000003278. PMID: 27124017Free PMC Article
Pareyson D, Marchesi C
Lancet Neurol 2009 Jul;8(7):654-67. doi: 10.1016/S1474-4422(09)70110-3. PMID: 19539237

Prognosis

Rossor AM, Reilly MM
Acta Neurol Scand 2022 Oct;146(4):325-331. Epub 2022 May 25 doi: 10.1111/ane.13650. PMID: 35611606Free PMC Article
Klein CJ
Continuum (Minneap Minn) 2020 Oct;26(5):1224-1256. doi: 10.1212/CON.0000000000000927. PMID: 33003000
Oprescu SN, Griffin LB, Beg AA, Antonellis A
Methods 2017 Jan 15;113:139-151. Epub 2016 Nov 20 doi: 10.1016/j.ymeth.2016.11.013. PMID: 27876679Free PMC Article
Pareyson D, Marchesi C
Lancet Neurol 2009 Jul;8(7):654-67. doi: 10.1016/S1474-4422(09)70110-3. PMID: 19539237
Casasnovas C, Cano LM, Albertí A, Céspedes M, Rigo G
Foot Ankle Spec 2008 Dec;1(6):350-4. Epub 2008 Oct 22 doi: 10.1177/1938640008326247. PMID: 19825739

Clinical prediction guides

Record CJ, Skorupinska M, Laura M, Rossor AM, Pareyson D, Pisciotta C, Feely SME, Lloyd TE, Horvath R, Sadjadi R, Herrmann DN, Li J, Walk D, Yum SW, Lewis RA, Day J, Burns J, Finkel RS, Saporta MA, Ramchandren S, Weiss MD, Acsadi G, Fridman V, Muntoni F, Poh R, Polke JM, Zuchner S, Shy ME, Scherer SS, Reilly MM; Inherited Neuropathies Consortium—Rare Disease Clinical Research Network
Brain 2023 Oct 3;146(10):4336-4349. doi: 10.1093/brain/awad187. PMID: 37284795Free PMC Article
Meyyazhagan A, Orlacchio A
Int J Mol Sci 2022 Feb 1;23(3) doi: 10.3390/ijms23031697. PMID: 35163618Free PMC Article
Klein CJ
Continuum (Minneap Minn) 2020 Oct;26(5):1224-1256. doi: 10.1212/CON.0000000000000927. PMID: 33003000
Oprescu SN, Griffin LB, Beg AA, Antonellis A
Methods 2017 Jan 15;113:139-151. Epub 2016 Nov 20 doi: 10.1016/j.ymeth.2016.11.013. PMID: 27876679Free PMC Article
Rinaldi R, Patel A
PM R 2013 May;5(5 Suppl):S63-73. Epub 2013 Mar 28 doi: 10.1016/j.pmrj.2013.03.028. PMID: 23542772

Recent systematic reviews

Finsterer J, Iglseder S, Wanschitz J, Topakian R, Löscher WN, Grisold W
Acta Neurol Scand 2019 Feb;139(2):92-105. Epub 2018 Oct 23 doi: 10.1111/ane.13035. PMID: 30295933
Corrado B, Ciardi G, Bargigli C
Medicine (Baltimore) 2016 Apr;95(17):e3278. doi: 10.1097/MD.0000000000003278. PMID: 27124017Free PMC Article
Barreto LC, Oliveira FS, Nunes PS, de França Costa IM, Garcez CA, Goes GM, Neves EL, de Souza Siqueira Quintans J, de Souza Araújo AA
Neuroepidemiology 2016;46(3):157-65. Epub 2016 Feb 6 doi: 10.1159/000443706. PMID: 26849231
Sman AD, Hackett D, Fiatarone Singh M, Fornusek C, Menezes MP, Burns J
J Peripher Nerv Syst 2015 Dec;20(4):347-62. doi: 10.1111/jns.12116. PMID: 26010435
Ruano L, Melo C, Silva MC, Coutinho P
Neuroepidemiology 2014;42(3):174-83. Epub 2014 Mar 5 doi: 10.1159/000358801. PMID: 24603320

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